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Rare disease market access live webinar: Strategic and tactical challenges facing orphan medicines entering Europe

In this webinar, we explored the challenges facing orphan medicines and other innovative rare disease treatments looking to achieve market access in Europe.

Orphan medicines and rare disease treatments are faced with a complex, ever-changing market landscape. These treatments also face unique tactical challenges on the route to securing market access.

Here we bring together specialists from our global market access (Rob Taaffe), systematic review (Regina Leadley), and health economic (Calum Jones) teams to explore this environment and some of the key hurdles that Pharmaceutical and Medtech innovators need to overcome in order to achieve patient access.

Rob, Regina and Calum discuss:

  • Current and future market events and trends for rare disease products across Europe
  • Clinical evidence development, including tactical challenges around evidence generation and how to address these
  • Building the health economic case, including key principles and tactical nuances for health economic modelling in rare and orphan disease

If you are launching a rare disease treatment or want to learn more about the market access journey for orphan medicines, email info@mtechaccess.co.uk to speak to our team.

Request a copy of the slides:

If you would like a copy of the slides used in our Rare Disease Market Access webinar, please submit your details here.

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    Meet our speakers:

    Rob Taaffe

    Rob Taaffe

    Associate Consultant, Global Market Access

    Regina Leadley

    Regina Leadley

    Consultant, Systematic Review

    Calum Jones

    Calum Jones

    Consultant, Health Economist

    Listen to the podcast:

    This episode is also available as a podcast. Listen below or search ‘Pharma Market Access Insights  – from Mtech Access’ on Spotify, Apple Podcasts or Google Podcasts.